Status: Finalised
First registered on:
08/07/2014
Last updated on:
02/08/2017
1. Study identification
EU PAS Register NumberEUPAS7023
Official titleDatabase study of lenalidomide (Revlimid®) in Germany: Monitoring off-label use
Study title acronym
Study typeObservational study
Brief description of the studyIn 2007 and 2008, lenalidomide, a derivate of thalidomide, was in combination with dexamethasone indicated for the treatment of multiple myeloma in patients who have received at least one prior therapy. In this study, based on claims data with around 14 million enrollees, off-label use of lenalidomide in Germany was considered. The study is part of a risk management plan required by EMA (European Medicines Agency) and the German Federal Institute for Drugs and Medical Devices (BfArM) due to the teratogenic potential of the drug.
Was this study requested by a regulator?Yes: Germany
Is the study required by a Risk Management Plan (RMP)?
EU RMP category 3 (required)
Regulatory procedure number (RMP Category 1 and 2 studies only)
Other study registration identification numbers and URLs as applicable
2. Research centres and Investigator details
Coordinating study entity
Centre to which the investigator belongsBIPS GmbH
Department/Research groupClinical Epidemiology
Organisation/affiliationLeibniz Inst. for Prevention Research and Epidem.
Details of (Primary) lead investigator
Title Dr
Last name Riedel
First name Oliver
Is this study being carried out with the collaboration of a research network?
No
Other centres where this study is being conducted
Not applicable (single centre)
Countries in which this study is being conducted
National study
Germany
3. Study timelines: initial administrative steps, progress reports and final report
PlannedActual
Date when funding contract was signed15/04/200815/04/2008
Start date of data collection06/05/200806/05/2008
Start date of data analysis08/05/200908/05/2009
Date of interim report, if expected05/05/201405/05/2014
Date of final study report31/12/201417/12/2014
4. Sources of funding
Please provide estimates of the percentage of funding by source for this study
Names(s)Approximate % funding
Pharmaceutical companiesCelgene GmbH100
Charities
Government body
Research councils
EU funding scheme
5. Contact details for enquiries
Scientific Enquiries
Title Dr
Last name Riedel
First name Oliver
Address line 1Achterstraße 30
Address line 2
Address line 3
CityBremen
Postcode
CountryGermany
Phone number (incl. country code)004942121856860
Alternative phone number
Fax number (incl. country code)
Public Enquiries
Title Dr
Last name Riedel
First name Oliver
Address line 1Achterstraße 30
Address line 2
Address line 3
CityBremen
Postcode
CountryGermany
Phone number (incl. country code)004942121856860
Alternative phone number
Fax number (incl. country code)
6. Study drug(s) information
Single-Constituent (Substance INN)LENALIDOMIDE
Product NameRevlimid
CountryGermany
Substance INN(s)LENALIDOMIDE
7. Medical conditions to be studied
Medical condition(s)Yes
Plasma cell myeloma
8. Population under study
Age
Adults (18 - 44 years)
Adults (45 - 64 years)
Adults (65 - 74 years)
Adults (75 years and over)
Sex
Male
Female
9. Number of subjects
Estimated total number of subjects500
Additional information
In 2008, 487 insurants fulfilled the eligibility criteria.
10. Source of data
Is this study being carried out with an established data source?Yes
Data sources registered with ENCePP
Sources of data
Administrative database, e.g. claims database
11. Scope of the study
What is the scope of the study?
Drug utilisation study
Primary scope : Drug utilisation study
12. Main objective(s)
What is the main objective of the study?
The objectives are to determine frequency and proportion of off-label use of lenalidomide by indication in 2008 and to investigate probable off label indications for lenalidomide. The initial dose of lenalidomide, dose changes and the number of lenalidomide dispensations per patient for on-label and off-label users were characterised. Incidence rates of lenalidomide use in 2008 were calculated.
Are there primary outcomes?Yes
frequency of off-label use
Are there secondary outcomes?No
13. Study design
What is the design of the study?
Cross-sectional study
Drug utilisation study
14. Follow-up of patients
Will patients be followed up?Not applicable/no follow-up
15. Data analysis plan
Please provide a brief summary of the analysis method
Descriptive analyses were conducted for all users of lenalidomide with respect to demographic characteristics, i.e. sex, age and federal state of residence, death and frequency of dispensations. Incidence rates of lenalidomide use by sex, age and federal state of residence were determined. Prevalence and incidence rates of lenalidomid use were calculated with 95% confidence intervals. Demographics and comorbidities are determined for patient with off-label use.
16. ENCePP seal
Are you requesting the ENCePP seal for this study?
No
17. Full protocol
Not submitted
18. Study Results
Not submitted
Please list the 5 most relevant publications using data from your study
ReferenceLink to web-publication
None
19. Other relevant documents
Conflict(s) of interest of
investigator(s)Not submitted
Composition of Steering Group and
ObserversNot submitted
Other documentsNot
submitted
Signed Code of
Conduct Checklist
Not submitted
Signed Code of Conduct Declaration
Not submitted
Signed Checklist for Study
Protocols
Not submitted
