Status: Finalised
First registered on:
21/01/2014
Last updated on:
15/11/2019
1. Study identification
EU PAS Register NumberEUPAS5599
Official titleAN OBSERVATIONAL POST-AUTHORIZATION MODIFIED PRESCRIPTION-EVENT MONITORING SAFETY STUDY TO MONITOR THE SAFETY AND UTILIZATION OF EXENATIDE ONCE WEEKLY (BYDUREON®) IN THE PRIMARY CARE SETTING IN ENGLAND
Study title acronym
Study typeObservational study
Brief description of the studyThis post-marketing Modified Prescription-Event Monitoring (M-PEM) safety study of exenatide (Bydureon®) is to be carried out as part of the Risk Management Plan required by the Committee for Medicinal Products for Human Use (CHMP) to further investigate the safety profile of Bydureon® in clinical practice. The aim of this study is to proactively capture safety and drug utilisation data in the post-marketing phase of license approval of Bydureon® as prescribed to patients by general practitioners in England. This M-PEM study will enable the systematic collection and reporting of drug utilisation and safety data on patients newly initiated on treatment with exenatide once weekly in the primary care setting. The study aims to collect exposure and outcome data for a cohort of approximately 5000 evaluable patients
Was this study requested by a regulator?Yes: EMA
Is the study required by a Risk Management Plan (RMP)?
EU RMP category 3 (required)
Regulatory procedure number (RMP Category 1 and 2 studies only)
Other study registration identification numbers and URLs as applicable
2. Research centres and Investigator details
Coordinating study entity
Centre to which the investigator belongsDSRU
Department/Research group
Organisation/affiliationDrug Safety Research Unit
Details of (Primary) lead investigator
Title Professor
Last name Shakir
First name Saad
Is this study being carried out with the collaboration of a research network?
No
Other centres where this study is being conducted
Not applicable (single centre)
Countries in which this study is being conducted
National study
United Kingdom
3. Study timelines: initial administrative steps, progress reports and final report
PlannedActual
Date when funding contract was signed23/02/2012
Start date of data collection02/09/201101/09/2011
Start date of data analysis02/04/201801/05/2018
Date of interim report, if expected01/12/201501/12/2015
Date of final study report01/11/201821/12/2018
4. Sources of funding
Please provide estimates of the percentage of funding by source for this study
Names(s)Approximate % funding
Pharmaceutical companiesEli Lilly &Co 36%, AstraZeneca 64%100
Charities
Government body
Research councils
EU funding scheme
5. Contact details for enquiries
Scientific Enquiries
Title Professor
Last name Shakir
First name Saad
Address line 1DSRU
Address line 2Bursledon Hall
Address line 3Blundell Lane
CitySouthampton
PostcodeSO31 1AA
CountryUnited Kingdom
Phone number (incl. country code)44-2380-408600
Alternative phone number
Fax number (incl. country code)44-2380-408609
Public Enquiries
Title Professor
Last name Shakir
First name Saad
Address line 1DSRU
Address line 2Bursledon Hall
Address line 3Blundell Lane
CitySouthampton
PostcodeSO31 1AA
CountryUnited Kingdom
Phone number (incl. country code)44-2380-408600
Alternative phone number
Fax number (incl. country code)44-2380-408609
6. Study drug(s) information
Product NameBydureon
CountryUnited Kingdom
Substance INN(s)EXENATIDE
7. Medical conditions to be studied
Medical condition(s)Yes
Type 2 diabetes mellitus
8. Population under study
Age
Adolescents (12 - 17 years)
Adults (18 - 44 years)
Adults (45 - 64 years)
Adults (65 - 74 years)
Adults (75 years and over)
Sex
Male
Female
9. Number of subjects
Estimated total number of subjects5000
10. Source of data
Is this study being carried out with an established data source?No
Sources of data
Prescription event monitoring
11. Scope of the study
What is the scope of the study?
Drug utilisation study
Safety
Primary scope : Safety
12. Main objective(s)
What is the main objective of the study?
To provide timely information to quantify the incidence rate of the important identified risk of acute pancreatitis in the first 12 months after starting treatment.
Are there primary outcomes?Yes
The incidence rate of the important identified risk of acute pancreatitis in the first 12 months after starting treatment
Are there secondary outcomes?Yes
1. The baseline health profile of patients on treatment with exenatide in the primary care setting, the treatment they received, and by whom
2. The risk profile of events reported in the 12 month observation period in the overall cohort and in special populations (arising from contraindications, precautions etc.)
13. Study design
What is the design of the study?
Prescription event monitoring
14. Follow-up of patients
Will patients be followed up?Yes
Please describe duration of follow up
If any of the following outcomes of interest are identified from responses to the main study questionnaire after 12 months of exposure, the prescriber will be contacted to obtain further details via a follow-up questionnaire: pregnancy, death, concomitant medication, certain events, adverse events.
15. Data analysis plan
Please provide a brief summary of the analysis method
PEM methodology provides a numerator (the number of reports of an event) and a denominator (the number of patient-months at risk), both collected within a known time frame. This allows for the calculation of risk (percent of total valid cohort exposed) and incidence densities (ID; person-time incidence rates) for each event. Such analyses will be performed using ‘Higher-level’ event terms from the MedDRA dictionary.
In addition, the incidence rate of acute pancreatitis will be explored in exenatide naïve and switcher patients by estimating the hazard rate of this event over time. The null hypothesis that the hazard rate of acute pancreatitis in patients exenatide will be constant during the 12 month exposure period following the start of treatment will be tested by fitting parametric time to event models (e.g. Weibull).
Descriptive summary statistics will also be employed to present such as demographic data.
16. ENCePP seal
Are you requesting the ENCePP seal for this study?
No
17. Full protocol
18. Study Results
Please list the 5 most relevant publications using data from your study
ReferenceLink to web-publication
None
19. Other relevant documents
Conflict(s) of interest of
investigator(s)Not submitted
Composition of Steering Group and
ObserversNot submitted
Other documentsNot
submitted
Signed Code of
Conduct Checklist
Not submitted
Signed Code of Conduct Declaration
Not submitted
Signed Checklist for Study
Protocols
Not submitted
