Status: Finalised
First registered on:
20/05/2019
Last updated on:
05/05/2020
1. Study identification
EU PAS Register NumberEUPAS29813
Official titleEvaluation of the Effectiveness of Risk Minimisation Measures: A Survey among Health Care Professionals to Assess their Knowledge on Dosing and Administration of Obizur® (Susoctocog alfa) in 6 European Countries
Study title acronym
Study typeOther: Survey
Brief description of the studyObizur® (susoctocog alfa) is indicated in adults for treatment of bleeding episodes in patients with acquired haemophilia caused by antibodies to Factor VIII (AHA).
The overall research question is to evaluate whether healthcare professionals (HCPs) expected to prescribe or dispense Obizur have been successfully informed by the educational materials regarding the method of calculation and administration of Obizur.
Study design: This is a cross-sectional, multinational web based survey conducted in 6 selected European countries (Belgium, Germany, Italy, Netherlands, Sweden, UK) among HCPs who treat patients with AHA and may be involved in prescribing, dose calculation, and dispensing of Obizur and were targeted to receive the educational materials.
Population
The study will be conducted among HCPs (physicians, nurses, pharmacists) who treat patients with AHA or may be involved in dose calculation or dispensing of Obizur.
Data Sources
The survey will involve primary data collection conducted through web questionnaire or phone.
In order to address the study objectives, the following information will be collected:
• Information on participating HCPs (demographics, HCP subgroup, specialty, setting)
• Information on participating HCPs’ awareness of the educational materials (recollecting receiving the educational materials, awareness of content, knowledge of content)
• For HCPs who have prescribed, calculated the dose of, or dispensed Obizur: information on patients (characteristics, administered and calculated dose, reasons for deviations from recommended dose).
Study Size
The target sample size for this study is 100 HCPs. Such a sample would allow the description of an unknown proportion of correct answers to any of the survey questions with a precision of 9.8% for a 95% confidence interval. Achievement of the sample size will depend on the number of HCPs who have received the educational materials.
Was this study requested by a regulator?No
Is the study required by a Risk Management Plan (RMP)?
EU RMP category 3 (required)
Regulatory procedure number (RMP Category 1 and 2 studies only)
Other study registration identification numbers and URLs as applicable
2. Research centres and Investigator details
Coordinating study entity
Centre to which the investigator belongsIQVIA
Department/Research groupReal World Insights
Organisation/affiliationIQVIA
Details of (Primary) lead investigator
Title Dr
Last name von Bredow
First name Dorothea
Is this study being carried out with the collaboration of a research network?
No
Other centres where this study is being conducted
Not applicable (single centre)
Countries in which this study is being conducted
International study
Belgium
Germany
Italy
Netherlands
Sweden
United Kingdom
3. Study timelines: initial administrative steps, progress reports and final report
PlannedActual
Date when funding contract was signed15/12/201715/12/2017
Start date of data collection01/07/201930/09/2019
Start date of data analysis15/01/202026/11/2019
Date of interim report, if expected
Date of final study report31/03/202006/03/2020
4. Sources of funding
Please provide estimates of the percentage of funding by source for this study
Names(s)Approximate % funding
Pharmaceutical companiesTakeda100
Charities
Government body
Research councils
EU funding scheme
5. Contact details for enquiries
Scientific Enquiries
Title Dr
Last name Page
First name Matt
Address line 1Takeda Pharmaceutical Company Limited
Address line 2650 East Kendall Street
Address line 3
CityCambridge
Postcode02142
CountryUnited States
Phone number (incl. country code)16175888613
Alternative phone number
Fax number (incl. country code)
Public Enquiries
Title Dr
Last name Page
First name Matt
Address line 1Takeda Pharmaceutical Company Limited
Address line 2650 East Kendall Street
Address line 3
CityCambridge
Postcode02142
CountryUnited States
Phone number (incl. country code)16175888613
Alternative phone number
Fax number (incl. country code)
6. Study drug(s) information
Product NameObizur
CountryGermany
Substance INN(s)SUSOCTOCOG ALFA
Product NameObizur
CountryBelgium
Substance INN(s)SUSOCTOCOG ALFA
Product NameObizur
CountryItaly
Substance INN(s)SUSOCTOCOG ALFA
Product NameObizur
CountryNetherlands
Substance INN(s)SUSOCTOCOG ALFA
Product NameObizur
CountrySweden
Substance INN(s)SUSOCTOCOG ALFA
Product NameObizur
CountryUnited Kingdom
Substance INN(s)SUSOCTOCOG ALFA
7. Medical conditions to be studied
Medical condition(s)No
8. Population under study
Age
Adults (18 - 44 years)
Adults (45 - 64 years)
Adults (65 - 74 years)
Adults (75 years and over)
Sex
Male
Female
9. Number of subjects
Estimated total number of subjects100
Additional information
This is a survey to evaluate whether healthcare professionals expected to prescribe or dispense Obizur have been successfully informed by the educational materials regarding the method of calculation and administration of Obizur. It is planned to include 100 health care professionals who have received the educational material.
10. Source of data
Is this study being carried out with an established data source?No
Sources of data
Survey of health care professionals; the number entered refers to the number of health care professionals, not to the number of patients
11. Scope of the study
What is the scope of the study?
Effectiveness evaluation
Primary scope : Effectiveness evaluation
12. Main objective(s)
What is the main objective of the study?
The overall research question is to evaluate whether healthcare professionals expected to prescribe or dispense Obizur have been successfully informed by the educational materials regarding the method of calculation and administration of Obizur.
Are there primary outcomes?Yes
Success rates will be determined:
Success if
o Proportion of HCPs remembering having received the educational materials ≥60% AND
o ≥80% of HCPs knowledgeable of the educational materials content AND
o Proportion of HCPs who would or did prescribe, calculate the dose of, or dispense Obizur in line with the educational materials ≥60%
Are there secondary outcomes?Yes
Success, if
•≥70% of HCPs remember having received the EM
• ≥70% HCPs are knowledgeable about the content of the EM
Success, if
•≥70%HCPs would prescribe, calculate the dose of, or dispense Obizur in line with the EM messages
•≥80% of HCPs did prescribe, calculate the dose of, or dispense Obizur in line with the EM by collecting self-reported dosing and dispensing information
13. Study design
What is the design of the study?
Cross-sectional study
14. Follow-up of patients
Will patients be followed up?Not applicable/no follow-up
15. Data analysis plan
Please provide a brief summary of the analysis method
Descriptive statistics will be applied. The endpoints will be assessed in overall, by country, and among different types of HCPs (physicians, pharmacists, nurses). Analyses by country will be performed in case if the number of HCPs per country will be >15.
Continuous variables will be described by their number (of valid cases, of missing values), mean, standard deviation, and median, Q1, Q3, minimum and maximum.
Categorical variables will be described as the total number and relative percentage per category. These will be the percentage per category.
Confidence intervals of 95% will be evaluated, when relevant.
The proportions of correct and appropriate answers to selected questions asked in the questionnaire will be expressed among HCPs who provided answers to those questions .
16. ENCePP seal
Are you requesting the ENCePP seal for this study?
No
17. Full protocol
Not submitted
18. Study Results
Not submitted
Please list the 5 most relevant publications using data from your study
ReferenceLink to web-publication
None
19. Other relevant documents
Conflict(s) of interest of
investigator(s)Not submitted
Composition of Steering Group and
ObserversNot submitted
Other documentsNot
submitted
Signed Code of
Conduct Checklist
Not submitted
Signed Code of Conduct Declaration
Not submitted
Signed Checklist for Study
Protocols
Not submitted
