Status: Finalised
First registered on:
25/03/2015
Last updated on:
14/01/2022
1. Study identification
EU PAS Register NumberEUPAS9097
Official titleAP24534-14-401: A Post-marketing Observational Registry to Evaluate the Incidence of and Risk Factors for Vascular Occlusive Events Associated with Iclusig® (Ponatinib) in Routine Clinical Practice in the US (OMNI)
Study title acronymOMNI
Study typeObservational study
Brief description of the studyA Post-marketing Observational Registry to Evaluate the Incidence of and Risk Factors for Vascular Occlusive Events Associated with Iclusig® (Ponatinib) in Routine Clinical Practice in the US (OMNI – Study Number AP24534-14-401)
Was this study requested by a regulator?Yes: United States
Is the study required by a Risk Management Plan (RMP)?
EU RMP category 3 (required)
Regulatory procedure number (RMP Category 1 and 2 studies only)
Other study registration identification numbers and URLs as applicable
2. Research centres and Investigator details
Coordinating study entity
Centre nameARIAD Pharmaceuticals, Inc (a wholly-owned subsidiary of Takeda Pharmaceuticals Company Limited)
Centre locationCambridge, MA, USA
Details of (Primary) lead investigator
Title Ms
Last name Stemhagen
First name Annette
Is this study being carried out with the collaboration of a research network?
No
Other centres where this study is being conducted
Not applicable (single centre)
Countries in which this study is being conducted
National study
United States
3. Study timelines: initial administrative steps, progress reports and final report
PlannedActual
Date when funding contract was signed07/11/2014
Start date of data collection01/12/201602/03/2018
Start date of data analysis19/02/2019
Date of interim report, if expected
Date of final study report30/11/202103/03/2021
4. Sources of funding
Please provide estimates of the percentage of funding by source for this study
Names(s)Approximate % funding
Pharmaceutical companiesARIAD Pharmaceuticals, Inc (a wholly-owned subsidiary of Takeda Pharmaceuticals Company Limited)100
Charities
Government body
Research councils
EU funding scheme
5. Contact details for enquiries
Scientific Enquiries
Title Ms
Last name Stemhagen
First name Annette
Address line 1United Biosource, LLC (UBC)
Address line 2920 Harvest Drive, Suite 200
Address line 3
CityBlue Bell, PA
Postcode19422
CountryUnited States
Phone number (incl. country code)12155912880
Alternative phone number
Fax number (incl. country code)
Public Enquiries
Title Ms
Last name Stemhagen
First name Annette
Address line 1United Biosource, LLC (UBC)
Address line 2920 Harvest Drive, Suite 200
Address line 3
CityBlue Bell, PA
Postcode19422
CountryUnited States
Phone number (incl. country code)12155912880
Alternative phone number
Fax number (incl. country code)
6. Study drug(s) information
Product NameIclusig
CountryUnited States
Substance INN(s)PONATINIB
7. Medical conditions to be studied
Medical condition(s)Yes
Vascular occlusion
8. Population under study
Age
Adults (18 - 44 years)
Adults (45 - 64 years)
Adults (65 - 74 years)
Adults (75 years and over)
Sex
Male
Female
Other population
Renal impaired
Hepatic impaired
Immunocompromised
9. Number of subjects
Estimated total number of subjects300
10. Source of data
Is this study being carried out with an established data source?No
Sources of data
Prospective patient-based data collection
11. Scope of the study
What is the scope of the study?
Risk assessment
Primary scope : Risk assessment
12. Main objective(s)
What is the main objective of the study?
The primary objectives of this study are to assess the following for patients with CP-CML AP-CML, BP-CML, or Ph+ ALL treated with Iclusig with or without anticoagulant and/or antiplatelet agents in routine clinical practice in the US:
· the incidence of vascular occlusive events (VOEs)
· the risk factors for development of VOEs
· the outcomes of VOEs
Are there primary outcomes?Yes
To evaluate the safety of Iclusig in routine care
Are there secondary outcomes?No
13. Study design
What is the design of the study?
Registry
14. Follow-up of patients
Will patients be followed up?Yes
Please describe duration of follow up
In case of treatment discontinuation at any time, data collection will continue on discontinued patients for a minimum of 12 months up to 30 months (total registry duration) from the patient's date of enrolment.
15. Data analysis plan
Please provide a brief summary of the analysis method
Analyses will include tabulations of the number of candidate patients identified and the
number of eligible patients per the inclusion/exclusion criteria. Baseline demographic and medical history data will be presented using descriptive statistics using number and percent for categorical endpoints, n, mean, SD, SE of the mean, median, minimum (min), and maximum (max) for continuous endpoints. The primary analyses will also present 95% CIs. Exploratory analyses will also be performed to better understand any differences in patients who experience any of the adverse events of special interest (VOEs) versus those who do not. The exploratory analyses will be performed using logistic regression, including factors such as patient demographic characteristics, risk factors, dose and duration of Iclusig treatment, and concomitant medications, including but not limited to prophylactic and/or therapeutic use of anticoagulant and/or antiplatelet agents.
16. ENCePP seal
Are you requesting the ENCePP seal for this study?
No
17. Full protocol
18. Study Results
Please list the 5 most relevant publications using data from your study
ReferenceLink to web-publication
None
19. Other relevant documents
Conflict(s) of interest of
investigator(s)Not submitted
Composition of Steering Group and
ObserversNot submitted
Other documentsNot
submitted
Signed Code of
Conduct Checklist
Not submitted
Signed Code of Conduct Declaration
Not submitted
Signed Checklist for Study
Protocols
Not submitted
